Most current treatment options, including antibiotics, pain medications, and blood transfusions, focus on preventing infections, relieving pain, and controlling complications as they occur; however, they do not affect how red blood cells work. Hydroxyurea and Endari (L-glutamine) are currently the only approved medications for the treatment of Sickle Cell Disease.

A bone marrow transplant is the only cure for Sickle Cell Disease; however, this risky procedure is available for a limited number of patients and may have serious side effects.

Because of the lack of treatments that target the underlying cause of sickle cell disease, people with Sickle Cell Disease often struggle with a range of severe symptoms, including severe pain crises, anemia, fatigue, frequent infections, and inflammation that start when they are infants and last a lifetime.

Help shape the future of Sickle Cell Disease.

Is a GBT HOPE clinical research study an option for you?